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      Switching to Glycerol Phenylbutyrate in 48 Patients with Urea Cycle Disorders: Clinical Experience in Spain 

      Martín Hernández, Elena; Quijada Fraile, Pilar; Correcher, Patricia; Meavilla, Silvia; Sánchez Pintos, Paula; De las Heras Montero, Javier Adolfo; Blasco Alonso, Javier; Dougherty, Lucy; Márquez, Ana; Peña Quintana, Luis; Cañedo, Elvira; García Jimenez, María Concepción; Moreno Lozano, Pedro Juan; Murray Hurtado, Mercedes; Camprodon Gómez, María; Barrio-Carreras, Delia; de los Santos, Mariela; del Toro, Mireia; Couce, María L.; Vitoria Miñana, Isidro; Morales Conejo, Montserrat; Bellusci, Marcello (MDPI, 2022-08-28)
      Background and objectives: Glycerol phenylbutyrate (GPB) has demonstrated safety and efficacy in patients with urea cycle disorders (UCDs) by means of its clinical trial program, but there are limited data in clinical ...